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Disease ReportsNeuronal ceroid-lipofuscinoses
MeSH D009472 - neuronal ceroid-lipofuscinoses
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Competitive Landscape
Events Timeline
Commercial
Clinical Trials
Competitive landscape
D008064:Lipidoses
0 Companies
0 Drugs
Success rate
D020271:Nervous system heredodegenerative disorders
0 Companies
0 Drugs
Success rate
D009472: 
Neuronal ceroid-lipofuscinoses
$
Success rate
Events Timeline
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Commercial
Company Name
Drug Name
Trade Name
Patent Expires
Approval Date
Revenue
Period
BioMarin PharmaceuticalCERLIPONASE ALFA Brineura  2017-04-27 $169.043 M Q3/23-Q2/24 
Clinical Trials
Historical Success Rate
Phase 1
100%
2/2
Phase 2
33%
2/6
Phase 3
50%
2/4
Approved: 2Overall Success rate: 17%
All Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Company name
Phase 1
Phase 2
Phase 3
Phase 4
Drug Name
BioMarin Pharmaceutical
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